Effect Size Analysis of Cipaglucosidase Alfa Plus Miglustat Versus Alglucosidase Alfa in ERT-experienced Adults with Late-onset Pompe Disease in PROPEL (S21.003).
Journal: Neurology
Year: February 20, 2025
Metabolic Geneticist
4.5
No OPD information available
Pompe Disease
3-Hydroxy-3-Methylglutaryl-CoA Lyase Deficiency
Addison's Disease
Adrenoleukodystrophy (ALD)
CACH Syndrome
Mucopolysaccharidoses (MPS)
Mucopolysaccharidosis Type 2 (MPS II, Hunter Syndrome)
Phenylketonuria (PKU)
Acid Sphingomyelinase Deficiency (ASMD)
Cardiomyopathy
Carnitine Palmitoyltransferase 1 Deficiency
Cutis Laxa
Fabry Disease
Gerodermia Osteodysplastica
Hereditary Hyperekplexia
High Blood Pressure in Infants
Infantile Neutropenia
Leigh Syndrome
Leukodystrophy
Long-Chain 3-Hydroxyacyl-CoA Dehydrogenase Deficiency
Metabolic Acidosis
Mitochondrial Trifunctional Protein Deficiency
Mucopolysaccharidosis Type 1 (MPS I, Hurler Syndrome)
Multiple Sulfatase Deficiency
Ornithine Transcarbamylase Deficiency
Rhabdomyolysis
Sideroblastic Anemia
Urea Cycle Disorders (UCD)
Von Gierke Disease
Drago Bratkovic is a male doctor who helps people with various rare diseases like Pompe Disease, Addison's Disease, and High Blood Pressure in Infants. He also works with conditions like Cardiomyopathy and Rhabdomyolysis. Drago has special skills in treating these complex health issues.
When Drago Bratkovic meets with patients, he talks to them in a kind and caring way. He listens to their concerns and explains things clearly. Patients trust him because he shows empathy and gives them hope for better health.
To stay updated with the latest medical knowledge, Drago reads research papers and attends conferences. This helps him provide the best care for his patients. He also collaborates with other doctors and shares his expertise to improve patient outcomes.
Drago Bratkovic's colleagues admire his dedication and teamwork. He values their input and works together with them to find the best solutions for patients. This collaborative approach ensures that patients receive comprehensive care.
Through his work, Drago has positively impacted many patients' lives. His research on Cipaglucosidase Alfa and Miglustat in Pompe Disease has led to better treatments for adults. In a clinical trial, he studied the safety and effectiveness of ATB200 in treating Pompe Disease, which has helped advance medical knowledge in this area.
In summary, Drago Bratkovic is a compassionate and knowledgeable doctor who specializes in rare diseases. He communicates effectively with patients, stays informed about the latest research, and collaborates with colleagues to provide the best care possible. His dedication to improving patients' lives through research and clinical trials makes him a respected figure in the medical community.
Journal: Neurology
Year: February 20, 2025
Enrollment Status: Completed
Published: September 19, 2024
Intervention Type: Drug
Study Drug:
Study Phase: Phase 1/Phase 2
Dr. Bratkovic is a fantastic Metabolic Geneticist who truly cares about his patients. He explained everything in a way that was easy to understand and made me feel at ease. Highly recommend!
Dr. Bratkovic is a top-notch Metabolic Geneticist. He was very thorough in his assessment and provided me with a clear treatment plan. I feel confident in his care.
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Dr. Bratkovic is an exceptional Metabolic Geneticist. He took the time to listen to my concerns and provided me with personalized recommendations. I feel fortunate to have found such a skilled doctor.
I had a wonderful experience with Dr. Bratkovic as my Metabolic Geneticist. He was professional, kind, and explained everything in a way that was easy to understand. Highly recommend his services.